OTX008 is primarily used in cancer research as a G-quadruplex stabilizing agent. It targets and binds to specific DNA structures found in the promoter regions of certain oncogenes, particularly the c-MYC gene, which is overexpressed in many cancers. By stabilizing these G-quadruplex structures, OTX008 suppresses the transcription of c-MYC, thereby inhibiting the growth and proliferation of tumor cells. It has shown promising activity in preclinical studies against various cancer types, including melanoma, leukemia, and solid tumors. Due to its ability to selectively interfere with cancer cell gene expression, OTX008 is being explored as a potential therapeutic agent in targeted anticancer strategies. Its application is mainly focused on molecular oncology research and the development of gene-targeted drugs.