Used to treat Gaucher disease type 1, a genetic disorder caused by the deficiency of an enzyme that breaks down fatty substances in the body. In this condition, harmful levels of lipids accumulate in organs like the liver, spleen, and bones. Eliglustat works by reducing the production of these lipids, helping to prevent their buildup. It is an oral medication that serves as a long-term maintenance therapy, improving symptoms such as enlarged organs, low blood cell counts, and bone pain. It is particularly suited for adults with specific genetic profiles and is often preferred over enzyme replacement therapy due to its convenience and effectiveness in eligible patients.