Used primarily in the treatment of lysosomal storage disorders, particularly Gaucher disease, by inhibiting glucosylceramide synthase. This action helps reduce the accumulation of glucosylceramide in cells, alleviating symptoms and improving patient outcomes. Additionally, it is researched for its potential antiviral properties, showing activity against certain viruses by interfering with glycosylation processes essential for viral replication. Its application extends to studies in diabetes management, where it may influence glucose metabolism and insulin sensitivity. Ongoing research explores its utility in other metabolic and genetic disorders, making it a compound of significant therapeutic interest.